Early research shows a one-time gene therapy has potential for addressing both the liver and lung disease that patients with ...
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Beam Base Editor’s Early Data in Rare Liver Disease Tee Up $500M Stock Sale in Tough MarketA Beam Therapeutics gene-editing therapy designed to fix a mutation at the root of a rare liver protein deficiency now has ...
Consequently, the mutant protein is entirely different due to the deletion of the fourth nucleotide, and it is also shorter due to the appearance of a premature stop codon. This mutant protein ...
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The protein that helps plants survive the coldThe protein she studied, PORCUPINE, was discovered because plants with a mutation in this gene became particularly ...
Fit Foods Ltd., a leading Canadian-based sports nutrition company in the bodybuilding and fitness industry for those born different, knows what drives the hardcore. Those who live for the ...
LETI-101 has demonstrated therapeutically relevant reductions of mutant huntingtin (HTT) protein, exceeding 80%, while preserving essential ...
The author is looking forward to seeing how Beam Therapeutics would do in their clinical trials of single-base DNA editing.
The one-time therapy appears to correct the mutation that causes the disease, known as Alpha-1 antitrypsin deficiency (AATD), ...
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