In 2025, Cellectis will continue to focus its efforts and expenses on advancing its core clinical trials BALLI-01 and NATHALI ...

HealthCare Pharmaceuticals was granted FDA orphan designation for a treatment of non-small cell lung cancer harboring epidermal ...

Caroline Wawira, from Embu, is seeking financial support to restart her life and provide for her kids after spending all her ...

PTC Therapeutics could boost revenue with vatiquinone for Friedreich's ataxia. Find out why PTCT stock is poised for growth ...

Allowing individuals to purchase a one-time “share” whose profits will fund ongoing financial assistance for these children ...

The University of Pretoria’s Giving Garden remains an advocate for food security as it has provided around 100 community food ...

Starfish Orphan Ministry is holding a Community Free Day from 9 a.m. to noon on Saturday, March 8. Everything is free, and everyone gets a 45-gallon bag to fill with ...

In their home in war-devastated Gaza City, Iman Farhat and her husband cherish the "paradise" brought by their newly-adopted ...

The FDA granted orphan drug status to rhenium-186 obisbemeda for treating leptomeningeal metastases in lung cancer.

Emapalumab-Izsg is under the FDA’s Priority Review for hemophagocytic lymphohistiocytosis/macrophage activation syndrome in Still disease.

EN001, a novel therapy under development by ENCell, has been granted Orphan Drug Designation by the U.S. FDA for the treatment of Charcot-Marie-Tooth (CMT) disease. Phase 1 clinical trial confirmed ...

The investigational immunotherapy bexmarilimab has been granted orphan drug designation from the FDA for patients with ...